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Convection-Enhanced Delivery of AAV Vector in Parkinsonian Monkeys; In Vivo Detection of Gene Expression and Restoration of Dopaminergic Function Using Pro-drug Approach

Experimental Neurology · 2000 · Vol. 164(1) · pp. 2–14
Krys S. BankiewiczJamie L. EberlingMałgorzata KohutnickaWilliam J. JagustPhillip PivirottoJohn R. BringasJanet CunninghamThomas F. BudingerJudith Harvey‐White
Virus-based gene therapy researchNerve injury and regenerationCRISPR and Genetic EngineeringDopamineDopaminergicCarbidopaGenetic enhancementStriatumGene deliveryNeuroscienceLevodopaTyrosine hydroxylaseParkinson's disease

MeSH terms

DependovirusAnimalsAromatic-L-Amino-Acid DecarboxylasesCarbidopaCatheterizationCaudate NucleusCell LineDopamineDrug Administration RoutesDrug CombinationsFluorine RadioisotopesGenetic VectorsLevodopaMacaca mulattaMagnetic Resonance Imaging
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FWCI
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37
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99%
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Convection-Enhanced Delivery of AAV Vector in Parkinsonian Monkeys; In Vivo Detection of Gene Expression and Restoration of Dopaminergic Function Using Pro-drug Approach · Scinovex