article Open AccessTop 1% cited
Early Treatment With Alglucosidase Alfa Prolongs Long-Term Survival of Infants With Pompe Disease
Pediatric Research · 2009 · Vol. 66(3) · pp. 329–335
Priya S. Kishnani✉(Duke University)Deya CorzoNancy D. Leslie(Cincinnati Children's Hospital Medical Center)Daniel Gruskin(University Medical Center)Ans van der Ploeg(Erasmus University Rotterdam)John Clancy(University of Alabama at Birmingham)Rossella Parini(University of Milano-Bicocca)Gilles Morin(Centre Hospitalier Universitaire Amiens-Picardie)Michael Beck(Universitätskinderklinik)Mislen Bauer(Boston Children's Hospital)Mikaël Jokic(Centre Hospitalier Universitaire de Caen)Chen-En Tsai(Buddhist Tzu Chi General Hospital)Brian W H Tsai(Chi Mei Medical Center)Claire MorganTara O’MearaSusan RichardsElisa TsaoHanna Mandel(Rambam Health Care Campus)
Lysosomal Storage Disorders ResearchGlycogen Storage Diseases and MyoclonusCarbohydrate Chemistry and SynthesisMedicineCardiomyopathyPediatricsVentilation (architecture)DiseaseInternal medicineSurgeryHeart failure
MeSH terms
alpha-GlucosidasesChildChild, PreschoolGlycogen Storage Disease Type IIHumansInfantRisk FactorsSurvival RateTreatment OutcomeKaplan-Meier Estimate
Funding
- Deutsches Krebsforschungszentrum
- National Institutes of Health
Citations
334
FWCI
11.30
field-weighted impact
References
20
Percentile
99%
vs. same field & year
Citations per year
References
A retrospective, multinational, multicenter study on the natural history of infantile-onset Pompe disease
The Journal of Pediatrics · 2006 · 580 citations
Regression Models and Life-Tables
Journal of the Royal Statistical Society Series B (Statistical Methodology) · 1972 · 38,926 citations
Nonparametric Estimation from Incomplete Observations
Journal of the American Statistical Association · 1958 · 38,793 citations
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